Long-term normalization in the central nervous system, ocular manifestations, and skeletal deformities by a single systemic adenovirus injection into neonatal mice with mucopolysaccharidosis VII
2003; Springer Nature; Volume: 10; Issue: 5 Linguagem: Inglês
10.1038/sj.gt.3301869
ISSN1476-5462
AutoresYusaku Kamata, Akiko Tanabe, Arihiko Kanaji, M Kosuga, Yasuyuki Fukuhara, X. -K. Li, Seiichi Suzuki, Masumi Yamada, Noriyuki Azuma, Torayuki Okuyama,
Tópico(s)Retinal Development and Disorders
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