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Evaluation of N-nonyl-deoxygalactonojirimycin as a pharmacological chaperone for human GM1 gangliosidosis leads to identification of a feline model suitable for testing enzyme enhancement therapy
2012; Elsevier BV; Volume: 107; Issue: 1-2 Linguagem: Inglês
10.1016/j.ymgme.2012.06.007
ISSN1096-7206
AutoresBrigitte Rigat, Michael B. Tropak, Justin Buttner, Ellen Crushell, Daphne Benedict, John W. Callahan, Douglas R. Martin, Don J. Mahuran,
Tópico(s)Cellular transport and secretion
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