Portal de Periódicos da CAPES

Treatment of Severe Combined Immunodeficiency Disease (SCID) due to Adenosine Deaminase Deficiency with CD34 + Selected Autologous Peripheral Blood Cells Transduced with a Human ADA Gene (Amendment). National Institutes of Health

1993; Mary Ann Liebert, Inc.; Volume: 4; Issue: 4 Linguagem: Inglês

10.1089/hum.1993.4.4-521

1557-7422

R. Michael Blaese, Kenneth W. Culver, W. French Anderson, Arthur W. Nienhuis, Cynthia E. Dunbar, Lauren A. Chang, Craig A. Mullen, Charles W. Carter, Susan F. Leitman, Melvin Berger, A. Dusty Miller, Richard Morgan, Thomas A. Fleisher, Roger Kobyashi, Ai Lan Kobyashi, Harvey G. Klein, Gene M. Shearer, Mario Clerici, Gerald Mcgarrity, Aliza Cassell,

Autoimmune and Inflammatory Disorders Research

Human Gene TherapyVol. 4, No. 4 News and CommentsTreatment of Severe Combined Immunodeficiency Disease (SCID) due to Adenosine Deaminase Deficiency with CD34+ Selected Autologous Peripheral Blood Cells Transduced with a Human ADA Gene (Amendment). National Institutes of HealthPRINCIPAL INVESTIGATOR R. Michael Blaese, ASSOCIATE INVESTIGATORS Kenneth W. Culver, W. French Anderson, Arthur Nienhuis, Cindy Dunbar, Lauren Chang, Craig Mullen, Charles Carter, Susan Leitman, OTHER CONTRIBUTORS Melvin Berger, A. Dusty Miller, Richard Morgan, Thomas Fleisher, Roger Kobyashi, Ai Lan Kobyashi, Harvey Klein, Gene Shearer, Mario Clerici, Gerald McGarrity, and Aliza CassellPRINCIPAL INVESTIGATOR R. Michael Blaese, ASSOCIATE INVESTIGATORS Kenneth W. Culver, W. French Anderson, Arthur Nienhuis, Cindy Dunbar, Lauren Chang, Craig Mullen, Charles Carter, Susan Leitman, OTHER CONTRIBUTORS Melvin Berger, A. Dusty Miller, Richard Morgan, Thomas Fleisher, Roger Kobyashi, Ai Lan Kobyashi, Harvey Klein, Gene Shearer, Mario Clerici, Gerald McGarrity, and Aliza CassellPublished Online:19 Mar 2008https://doi.org/10.1089/hum.1993.4.4-521AboutSectionsPDF/EPUB ToolsPermissionsDownload CitationsTrack CitationsAdd to favorites Back To Publication ShareShare onFacebookTwitterLinked InRedditEmail FiguresReferencesRelatedDetailsCited ByUsing analogue data to substantiate long-term durability of gene therapies: a narrative reviewRegenerative Medicine, Vol. 17, No. 10Advances in the treatment of severe combined immunodeficiencyClinical Immunology, Vol. 242In Utero Gene Therapy for Primary Immunodeficiencies6 September 2021 | Clinical Obstetrics & Gynecology, Vol. 64, No. 4Gene therapy using haematopoietic stem and progenitor cells10 December 2020 | Nature Reviews Genetics, Vol. 22, No. 4Consensus approach for the management of severe combined immune deficiency caused by adenosine deaminase deficiencyJournal of Allergy and Clinical Immunology, Vol. 143, No. 3Gene therapy for sickle cell disease: An updateCytotherapy, Vol. 20, No. 7Deliverable transgenics & gene therapy possibilities for the testesMolecular and Cellular Endocrinology, Vol. 468Lancet Commission: Stem cells and regenerative medicineThe Lancet, Vol. 391, No. 10123Long-Term Safety Follow-Up of Subjects Previously Treated with Non-Replicating Retroviral Vector-Based Gene Therapies19 July 2016 | Molecular Diagnosis & Therapy, Vol. 20, No. 6Twenty years of the International Society for Cellular Therapies: the past, present and future of cellular therapy clinical developmentCytotherapy, Vol. 16, No. 4Phoenix rising: gene therapy makes a comeback23 May 2012 | Acta Biochimica et Biophysica Sinica, Vol. 44, No. 8Lessons from Genetically Altered Mesenchymal Stem Cells (MSCs): Candidates for Improved MSC-Directed Myocardial Repair1 June 2012 | Cell Transplantation, Vol. 21, No. 6Nucleic-acid based gene therapeutics: delivery challenges and modular design of nonviral gene carriers and expression cassettes to overcome intracellular barriers for sustained targeted expression6 February 2012 | Journal of Drug Targeting, Vol. 20, No. 4Retroviral and Lentiviral Vectors for the Induction of Immunological ToleranceScientifica, Vol. 2012Introduction to Gene Therapy22 March 2012Gene and cell therapy based treatment strategies for inflammatory bowel diseasesWorld Journal of Gastrointestinal Pathophysiology, Vol. 2, No. 6In vivo expansion of MDR1-transduced cells accompanied by a post-transplantation chemotherapy regimen with mitomycin C and methotrexate8 June 2010 | The Journal of Gene Medicine, Vol. 12, No. 7Lentiviral Vectors in Gene Therapy: Their Current Status and Future Potential9 February 2010 | Archivum Immunologiae et Therapiae Experimentalis, Vol. 58, No. 2Cancer, chitosan nanoparticles and catalytic nucleic acids8 January 2010 | Journal of Pharmacy and Pharmacology, Vol. 61, No. 1Gene Therapy: Design and Prospects for Craniofacial Regeneration29 July 2009 | Journal of Dental Research, Vol. 88, No. 7A Roadmap to Safe, Efficient, and Stable Lentivirus-Mediated Gene Therapy with Hematopoietic Cell TransplantationBiology of Blood and Marrow Transplantation, Vol. 13, No. 12Cellular Therapies: A Canadian Blood Services Research and Development SymposiumTransfusion Medicine Reviews, Vol. 21, No. 4Prospects for Gene Therapy for Brain TumorsWhat can cardiovascular gene transfer learn from genomics: and vice versa?Physiological Genomics, Vol. 11, No. 3Dangerous liaisons: the role of "danger" signals in the immune response to gene therapyBlood, Vol. 100, No. 4Somatic Gene Therapy, Paradigm Shift or Pandora's BoxGene Therapy22 July 2014 | The Journal of Dermatology, Vol. 28, No. 4Terapia génica en células madre hematopoyéticas: mitos y realidadesMedicina Clínica, Vol. 117, No. 20Expansion and Fibronectin-Enhanced Retroviral Transduction of Primary Human T Lymphocytes for Adoptive ImmunotherapyT-Bodies as Antiviral AgentsGene therapy for Canavan disease?1 January 2001 | Annals of Neurology, Vol. 48, No. 1Gene therapy for Canavan disease?1 January 2001 | Annals of Neurology, Vol. 48, No. 1LYMPHOID CELLSGene therapy for inflammatory diseases of the salivary glandsProtection by Various Deoxynucleosides against Deoxyadenosine-Induced DNA Damage in Adenosine Deaminase-Inactivated LymphocytesMolecular Genetics and Metabolism, Vol. 68, No. 4A Phase I Trial of Autologous CD34+ Hematopoietic Progenitor Cells Transduced with an Anti-HIV Ribozyme6 July 2004 | Human Gene Therapy, Vol. 10, No. 13Transfert génique à visée thérapeutique dans les cellules souches hématopoïétiques et les cellules du système immunitaireAnnales de l'Institut Pasteur / Actualités, Vol. 10, No. 3-4Potential use of T cell receptor genes to modify hematopoietic stem cells for the gene therapy of cancerPathology & Oncology Research, Vol. 5, No. 1Mobilization and Transduction of Peripheral Blood Progenitor Cells in Patients with Mucopolysaccharidosis I27 March 2009 | Journal of Hematotherapy, Vol. 7, No. 6HIV, but not murine leukemia virus, vectors mediate high efficiency gene transfer into freshly isolated G 0 /G 1 human hematopoietic stem cells29 September 1998 | Proceedings of the National Academy of Sciences, Vol. 95, No. 20Retroviral gene transfer into cord blood stem/progenitor cells using purified vector stocksAmerican Journal of Hematology, Vol. 57, No. 1Adenosine modulates cell proliferation in human colonic adenocarcinoma. I. Possible involvement of adenosine A1 receptor subtypes in HT29 cellsEuropean Journal of Pharmacology, Vol. 341, No. 2-3Retroviral gene transfer into cord blood stem/progenitor cells using purified vector stocksAmerican Journal of Hematology, Vol. 57, No. 1GENETIC THERAPYPediatric Clinics of North America, Vol. 44, No. 1Retroviral gene therapy in hematopoietic diseasesJournal of Clinical Apheresis, Vol. 12, No. 4Retroviral gene therapy in hematopoietic diseasesJournal of Clinical Apheresis, Vol. 12, No. 4Retroviral gene therapy in hematopoietic diseasesJournal of Clinical Apheresis, Vol. 12, No. 4Retroviral gene therapy in hematopoietic diseasesJournal of Clinical Apheresis, Vol. 12, No. 4Gene therapy in surgeryEuropean Surgery, Vol. 29, No. 1Gene transfer into hematopoietic stem cellsTransfusion Science, Vol. 17, No. 1T–cell mediated rejection of gene–modified HIV–specific cytotoxic T lymphocytes in HIV–infected patients1 February 1996 | Nature Medicine, Vol. 2, No. 2Special Section: Autologous Stem Cell Tranplantations in Solid Tumours: Autologous Stem Cell Transplants in Lymphomas8 July 2009 | Annals of Medicine, Vol. 28, No. 2Investigations of Retroviral-Mediated Gene Therapy for Malignant Glioma: Transduction with HTK-Bearing Retroviruses Sensitizes Glioma Cells to GanciclovirExpression of the APC gene after transfection into a colonic cancer cell line.Gut, Vol. 37, No. 6Infectious Retrovirus Is Inactivated by Serum but Not by Cerebrospinal Fluid or Fluid from Tumor Bed in Patients with Malignant Glioma24 August 2005 | Japanese Journal of Cancer Research, Vol. 86, No. 11Porphyrie érythropoïétique congénitale. À propos d'un cas fatal en période néonatale dûà une hémolyse aiguë avec insuffisance hépatiqueArchives de Pédiatrie, Vol. 2, No. 8Protection of Retroviral Vector Particles in Human Blood Through Complement Inhibition19 March 2008 | Human Gene Therapy, Vol. 6, No. 4Porphyrias: Animal models and prospects for cellular and gene therapyJournal of Bioenergetics and Biomembranes, Vol. 27, No. 2Gene therapy for inherited disordersJournal of Pediatric Nursing, Vol. 10, No. 1Cellular Gene TherapyHematology/Oncology Clinics of North America, Vol. 9, No. 1Autologous Bone Marrow Transplantation27 September 2008 | Critical Reviews in Clinical Laboratory Sciences, Vol. 32, No. 1Biochemical and Immunological Status Following Gene Therapy and PEG-ADA Therapy for Adenosine Deaminase (ADA) DeficiencyAIDS and HIV infection Volume 4Issue 4Aug 1993 InformationCopyright 1993, Mary Ann Liebert, Inc.To cite this article:PRINCIPAL INVESTIGATOR R. Michael Blaese, ASSOCIATE INVESTIGATORS Kenneth W. Culver, W. French Anderson, Arthur Nienhuis, Cindy Dunbar, Lauren Chang, Craig Mullen, Charles Carter, Susan Leitman, OTHER CONTRIBUTORS Melvin Berger, A. Dusty Miller, Richard Morgan, Thomas Fleisher, Roger Kobyashi, Ai Lan Kobyashi, Harvey Klein, Gene Shearer, Mario Clerici, Gerald McGarrity, and Aliza Cassell.Treatment of Severe Combined Immunodeficiency Disease (SCID) due to Adenosine Deaminase Deficiency with CD34+ Selected Autologous Peripheral Blood Cells Transduced with a Human ADA Gene (Amendment). National Institutes of Health.Human Gene Therapy.Aug 1993.521-527.http://doi.org/10.1089/hum.1993.4.4-521Published in Volume: 4 Issue 4: March 19, 2008PDF download