Enzyme replacement therapy with alglucosidase alfa in 44 patients with late-onset glycogen storage disease type 2: 12-month results of an observational clinical trial
2009; Springer Science+Business Media; Volume: 257; Issue: 1 Linguagem: Inglês
10.1007/s00415-009-5275-3
ISSN1432-1459
AutoresS. Strothotte, N. Strigl‐Pill, Birgit Grunert, Cornelia Kornblum, K. Eger, Carsten Wessig, Marcus Deschauer, Frank Breunig, Franz X. Glocker, Stefan Vielhaber, Andrea Brejova, Max J. Hilz, Karlheinz Reiners, Wolfgang Müller‐Felber, Eugen Mengel, Matthias Spranger, Benedikt Schoser,
Tópico(s)Carbohydrate Chemistry and Synthesis
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