Enzyme replacement therapy in two patients with an advanced severe (Hurler) phenotype of mucopolysaccharidosis I
2006; Springer Science+Business Media; Volume: 166; Issue: 7 Linguagem: Inglês
10.1007/s00431-006-0316-8
ISSN1432-1076
AutoresVišnja Tokić, Ingeborg Barišić, Nevenka Huzjak, Giorgie Petković, Ksenija Fumić, Eduard Paschke,
Tópico(s)Parkinson's Disease Mechanisms and Treatments
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