Therapeutic silencing of an endogenous gene by systemic administration of modified siRNAs
2004; Nature Portfolio; Volume: 432; Issue: 7014 Linguagem: Inglês
10.1038/nature03121
ISSN1476-4687
AutoresJürgen Soutschek, Akin Akinc, Birgit Bramlage, Klaus Charissé, Rainer Constien, Mary Donoghue, Sayda M. Elbashir, Anke Geick, Philipp Hadwiger, Jens Harborth, Matthias John, Venkitasamy Kesavan, Gary Lavine, Rajendra K. Pandey, Timothy Racie, Kallanthottathil G. Rajeev, Ingo Röhl, Ivanka Toudjarska, Gang Wang, Silvio Wuschko, David Bumcrot, Victor Koteliansky, Stefan Limmer, Muthiah Manoharan, Hans‐Peter Vornlocher,
Tópico(s)MicroRNA in disease regulation
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