Artigo Acesso aberto Revisado por pares

Familial Hyperinsulinism Caused by an Activating Glucokinase Mutation

1998; Massachusetts Medical Society; Volume: 338; Issue: 4 Linguagem: Inglês

10.1056/nejm199801223380404

ISSN

1533-4406

Autores

Benjamin Gläser, Prebakaran Kesavan, Mozhgan Heyman, Elizabeth A. Davis, Antonio L. Cuesta, Andreas Buchs, Charles A. Stanley, Paul Thornton, M. Alan Permutt, Franz M. Matschinsky, Kevan C. Herold,

Tópico(s)

Cancer, Hypoxia, and Metabolism

Resumo

Spontaneous hyperinsulinemic hypoglycemia in adults is most frequently caused by sporadic, solitary pancreatic beta-cell tumors, whereas hyperinsulinemic hypoglycemia in childhood is commonly caused by generalized beta-cell dysfunction.1 Mutations in the beta-cell sulfonylurea-receptor (SUR1) gene or inward-rectifying potassium-channel (Kir6.2) gene were found in some patients.2–7 A distinct syndrome of hyperinsulinism with hyperammonemia was recently described,8,9 apparently caused by mutations in the glutamate dehydrogenase gene.10 However, many sporadic and familial cases of hyperinsulinism remain unexplained. Some may be due to somatic mutations in other genes, as suggested by reports of autosomal dominant familial hyperinsulinism that was . . .

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