Voltar
Artigo Acesso aberto Revisado por pares
BIBTEX RIS

Lentiviral hematopoietic stem cell gene therapy for X-linked severe combined immunodeficiency

2016; American Association for the Advancement of Science; Volume: 8; Issue: 335 Linguagem: Inglês

10.1126/scitranslmed.aad8856

ISSN

1946-6242

Autores

Suk See De Ravin, Xiaolin Wu, Susan Moir, Lela Kardava, Sandra Anaya‐O’Brien, Nana Kwatemaa, Patricia Littel, Narda Theobald, Uimook Choi, Ling Su, Martha Marquesen, Dianne Hilligoss, Janet Lee, Clarissa M. Buckner, Kol A. Zarember, Geraldine M. O’Connor, Daniel W. McVicar, Douglas B. Kuhns, Robert E. Throm, Sheng Zhou, Luigi D. Notarangelo, I. Celine Hanson, Mort J. Cowan, Elizabeth M. Kang, Coleen Hadigan, Michael M. Meagher, John T. Gray, Brian P. Sorrentino, Harry L. Malech,

Tópico(s)

CRISPR and Genetic Engineering

Resumo

Lentiviral gene therapy with conditioning achieves humoral reconstitution in older SCID-X1 patients.

Referência(s)