Drug discovery for Diamond-Blackfan anemia using reprogrammed hematopoietic progenitors
2017; American Association for the Advancement of Science; Volume: 9; Issue: 376 Linguagem: Inglês
10.1126/scitranslmed.aah5645
ISSN1946-6242
AutoresSergei Doulatov, Linda T. Vo, Elizabeth R. Macari, Lara Wahlster, Melissa A. Kinney, Alison M. Taylor, Jessica Barragan, Manav Gupta, Katherine McGrath, Hsiang‐Ying Lee, Jessica M. Humphries, Alexander L. DeVine, Anupama Narla, Blanche P. Alter, Alan H. Beggs, Suneet Agarwal, Benjamin L. Ebert, Hanna T. Gazda, Harvey F. Lodish, Colin A. Sieff, Thorsten M. Schlaeger, Leonard I. Zon, George Q. Daley,
Tópico(s)Epigenetics and DNA Methylation
ResumoA stem cell reprogramming approach enables disease modeling and drug discovery for a genetic blood disorder and uncovers a candidate therapeutic.
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