Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia
2019; Nature Portfolio; Volume: 25; Issue: 9 Linguagem: Inglês
10.1038/s41591-019-0550-z
ISSN1546-170X
AutoresPaula Rı́o, Susana Navarro, Wei Wang, Rebeca Sánchez‐Domínguez, Roser Pujol, José C. Segovia, Massimo Bogliolo, Eva Merino, Ning Wu, Rocío Salgado, María L. Lamana, Rosa María Pérez Yáñez, José Antonio Casado, Yari Giménez, Francisco J Roman‐Rodriguez, Lara Álvarez, Omaira Alberquilla, Anna Raimbault, Guillermo Güenechea, M. Luz Lozano, Laura Cerrato, Miriam Hernando-Rodríguez, Eva Heredero Gálvez, Raquel Hladun, Irina Giralt, Jordi Barquinero, Anne Galy, Nagore García de Andoín, Ricardo López Almaraz, Albert Catalá, Jonathan D. Schwartz, Jordi Surrallés, Jean Soulier, Manfred Schmidt, Cristina Díaz de Heredia, Julián Sevilla, Juan A. Bueren,
Tópico(s)Genetic Neurodegenerative Diseases
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