Selumetinib in Children with Inoperable Plexiform Neurofibromas
2020; Massachusetts Medical Society; Volume: 382; Issue: 15 Linguagem: Inglês
10.1056/nejmoa1912735
ISSN1533-4406
AutoresAndrea M. Gross, Pamela L. Wolters, Eva Dombi, Andrea Baldwin, Patricia Whitcomb, Michael J. Fisher, Brian Weiss, AeRang Kim, Miriam Bornhorst, Amish C. Shah, Staci Martin, Marie Claire Roderick, Dominique C. Pichard, Amanda Carbonell, Scott M. Paul, Janet Therrien, Oxana B. Kapustina, Kara Heisey, D. Wade Clapp, Chi Zhang, Cody J. Peer, William D. Figg, Malcolm A. Smith, John Glod, Jaishri O. Blakeley, Seth M. Steinberg, David Venzon, L. Austin Doyle, Brigitte C. Widemann,
Tópico(s)Management of metastatic bone disease
ResumoNo approved therapies exist for inoperable plexiform neurofibromas in patients with neurofibromatosis type 1.
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