Artigo Acesso aberto Revisado por pares

Selumetinib in Children with Inoperable Plexiform Neurofibromas

2020; Massachusetts Medical Society; Volume: 382; Issue: 15 Linguagem: Inglês

10.1056/nejmoa1912735

ISSN

1533-4406

Autores

Andrea M. Gross, Pamela L. Wolters, Eva Dombi, Andrea Baldwin, Patricia Whitcomb, Michael J. Fisher, Brian Weiss, AeRang Kim, Miriam Bornhorst, Amish C. Shah, Staci Martin, Marie Claire Roderick, Dominique C. Pichard, Amanda Carbonell, Scott M. Paul, Janet Therrien, Oxana B. Kapustina, Kara Heisey, D. Wade Clapp, Chi Zhang, Cody J. Peer, William D. Figg, Malcolm A. Smith, John Glod, Jaishri O. Blakeley, Seth M. Steinberg, David Venzon, L. Austin Doyle, Brigitte C. Widemann,

Tópico(s)

Management of metastatic bone disease

Resumo

No approved therapies exist for inoperable plexiform neurofibromas in patients with neurofibromatosis type 1.

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