Effectiveness of emicizumab in preventing life‐threatening bleeding complications in type 3 von Willebrand disease with inhibitors: A paediatric report
2020; Wiley; Volume: 27; Issue: 4 Linguagem: Inglês
10.1111/hae.14209
ISSN1365-2516
AutoresMaria Giuseppina Cefalo, Francesca Ronco, Giovina Di Felice, Martina Rinelli, Vincenzo Oriana, Michela Massoud, Pietro Merli, Matteo Luciani,
Tópico(s)Blood Coagulation and Thrombosis Mechanisms
ResumoHaemophiliaVolume 27, Issue 4 p. e495-e497 LETTER TO THE EDITOR Effectiveness of emicizumab in preventing life-threatening bleeding complications in type 3 von Willebrand disease with inhibitors: A paediatric report Maria Giuseppina Cefalo, Maria Giuseppina Cefalo Bambino Gesù Pediatric Hospital, Roma, Italy Azienda Ospedaliera Bianchi-Melacrino-Morelli, Reggio Calabria, ItalySearch for more papers by this authorFrancesca Ronco, Francesca Ronco Bambino Gesù Pediatric Hospital, Roma, Italy Azienda Ospedaliera Bianchi-Melacrino-Morelli, Reggio Calabria, ItalySearch for more papers by this authorGiovina Di Felice, Giovina Di Felice Bambino Gesù Pediatric Hospital, Roma, Italy Azienda Ospedaliera Bianchi-Melacrino-Morelli, Reggio Calabria, ItalySearch for more papers by this authorMartina Rinelli, Martina Rinelli Bambino Gesù Pediatric Hospital, Roma, Italy Azienda Ospedaliera Bianchi-Melacrino-Morelli, Reggio Calabria, ItalySearch for more papers by this authorVincenzo Oriana, Vincenzo Oriana Bambino Gesù Pediatric Hospital, Roma, Italy Azienda Ospedaliera Bianchi-Melacrino-Morelli, Reggio Calabria, ItalySearch for more papers by this authorMichela Massoud, Michela Massoud Bambino Gesù Pediatric Hospital, Roma, Italy Azienda Ospedaliera Bianchi-Melacrino-Morelli, Reggio Calabria, ItalySearch for more papers by this authorPietro Merli, Pietro Merli Bambino Gesù Pediatric Hospital, Roma, Italy Azienda Ospedaliera Bianchi-Melacrino-Morelli, Reggio Calabria, ItalySearch for more papers by this authorMatteo Luciani, Corresponding Author Matteo Luciani matteo.luciani@opbg.net orcid.org/0000-0002-6939-3047 Bambino Gesù Pediatric Hospital, Roma, Italy Azienda Ospedaliera Bianchi-Melacrino-Morelli, Reggio Calabria, Italy Correspondence Matteo Luciani, Onco-Hematology, Cell and Gene Therapy and Hematopoietic Transplantation Department, Bambino Gesù Pediatric Hospital, Piazza S. Onofrio 4, 00165 Rome, Italy. Email: matteo.luciani@opbg.netSearch for more papers by this author Maria Giuseppina Cefalo, Maria Giuseppina Cefalo Bambino Gesù Pediatric Hospital, Roma, Italy Azienda Ospedaliera Bianchi-Melacrino-Morelli, Reggio Calabria, ItalySearch for more papers by this authorFrancesca Ronco, Francesca Ronco Bambino Gesù Pediatric Hospital, Roma, Italy Azienda Ospedaliera Bianchi-Melacrino-Morelli, Reggio Calabria, ItalySearch for more papers by this authorGiovina Di Felice, Giovina Di Felice Bambino Gesù Pediatric Hospital, Roma, Italy Azienda Ospedaliera Bianchi-Melacrino-Morelli, Reggio Calabria, ItalySearch for more papers by this authorMartina Rinelli, Martina Rinelli Bambino Gesù Pediatric Hospital, Roma, Italy Azienda Ospedaliera Bianchi-Melacrino-Morelli, Reggio Calabria, ItalySearch for more papers by this authorVincenzo Oriana, Vincenzo Oriana Bambino Gesù Pediatric Hospital, Roma, Italy Azienda Ospedaliera Bianchi-Melacrino-Morelli, Reggio Calabria, ItalySearch for more papers by this authorMichela Massoud, Michela Massoud Bambino Gesù Pediatric Hospital, Roma, Italy Azienda Ospedaliera Bianchi-Melacrino-Morelli, Reggio Calabria, ItalySearch for more papers by this authorPietro Merli, Pietro Merli Bambino Gesù Pediatric Hospital, Roma, Italy Azienda Ospedaliera Bianchi-Melacrino-Morelli, Reggio Calabria, ItalySearch for more papers by this authorMatteo Luciani, Corresponding Author Matteo Luciani matteo.luciani@opbg.net orcid.org/0000-0002-6939-3047 Bambino Gesù Pediatric Hospital, Roma, Italy Azienda Ospedaliera Bianchi-Melacrino-Morelli, Reggio Calabria, Italy Correspondence Matteo Luciani, Onco-Hematology, Cell and Gene Therapy and Hematopoietic Transplantation Department, Bambino Gesù Pediatric Hospital, Piazza S. Onofrio 4, 00165 Rome, Italy. Email: matteo.luciani@opbg.netSearch for more papers by this author First published: 20 November 2020 https://doi.org/10.1111/hae.14209Citations: 3Read the full textAboutPDF ToolsRequest permissionExport citationAdd to favoritesTrack citation ShareShare Give accessShare full text accessShare full-text accessPlease review our Terms and Conditions of Use and check box below to share full-text version of article.I have read and accept the Wiley Online Library Terms and Conditions of UseShareable LinkUse the link below to share a full-text version of this article with your friends and colleagues. Learn more.Copy URL Share a linkShare onFacebookTwitterLinkedInRedditWechat No abstract is available for this article.Citing Literature Volume27, Issue4July 2021Pages e495-e497 RelatedInformation
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