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Artigo Revisado por pares
BIBTEX RIS

Patient and physician perspectives inform clinical trial design for a single intravenous dose of HMI-203, a gene therapy candidate for adults with mucopolysaccharidosis type II (MPS II, Hunter syndrome)

2022; Elsevier BV; Volume: 135; Issue: 2 Linguagem: Inglês

10.1016/j.ymgme.2021.11.133

ISSN

1096-7206

Autores

Jeffrey A Haroldson, Cj Witalisz, Cara Mayfield, N. Matthew Ellinwood, Leslie Urdaneta, Rick Martin, Gabriel Cohn,

Tópico(s)

Autism Spectrum Disorder Research

Referência(s)