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The burden of illness of patients with paroxysmal nocturnal haemoglobinuria receiving C5 inhibitors in France, Germany and the United Kingdom: Patient‐reported insights on symptoms and quality of life

2022; Wiley; Volume: 109; Issue: 4 Linguagem: Inglês

10.1111/ejh.13816

1600-0609

Jens Panse, Flore Sicre de Fontbrune, Pascale Burmester, Maria Piggin, Joana E. Matos, Halley Costantino, Koo Wilson, Zalmaï Hakimi, Jameel Nazir, Renaud Desgraz, Jesse Fishman, Emmelie Persson, Austin Kulasekararaj,

Blood groups and transfusion

To assess the clinical, humanistic and economic burden of paroxysmal nocturnal haemoglobinuria (PNH) among C5 inhibitor (C5i)-treated patients with PNH.