Dystrophin Immunity after Gene Therapy for Duchenne’s Muscular Dystrophy
2023; Massachusetts Medical Society; Volume: 388; Issue: 24 Linguagem: Inglês
10.1056/nejmc2212912
ISSN1533-4406
AutoresCarsten G. Bönnemann, Beth A. Belluscio, Serge Braun, Carl Morris, Teji Singh, Francesco Muntoni,
Tópico(s)Neuroscience and Neural Engineering
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