Impact of Vutrisiran on Quality of Life and Physical Function in Patients with Hereditary Transthyretin-Mediated Amyloidosis with Polyneuropathy

Adis, Springer Healthcare;

Autores

Laura Obici, Senda Ajroud‐Driss, Kon‐Ping Lin, John L. Berk, Julian D. Gillmore, Parag Kale, Haruki Koike, David Danese, Emre Aldinc, Chongshu Chen, Joshua R. Vest, David Adams, Jonas Wixner, Rolf Backlund, Björn Pilebro, Intissar Anan, Fredrik Edbom, Anna Ekman, Sandra Arvidsson, Ulrika H. Englund, Karin Söderberg, Erik Nordh, Erica Uneus, Kristin Samuelsson, A Nilzén, Rayomand Press, Mirjam Bilecen, Teresa Coelho, Marta Novais, Patrícia Rodrigues, Ana Martins da Silva, Inês Lopes Cardoso, Carla Rodrigues, Joana Ramalho, Helder Martins, Mónica G. Silva, Nádia Guimarães, Javier Martínez Pérez, Antonio Hipólito Reis, Julia R Monte, Natália Ferreira, Cristina Alves, Márcio Cardoso, Ricardo Cotrin Teixeira, Isabel Conceição, Filipa Lamas, Miguel Oliveira Santos, Catarina Falcão de Campos, Conceição de Azevedo Coutinho, José Castro, Isabel Castro, Daniela Rodrigues Silva, Susana Gonçalves, Eleonora Di Buduo, Claudia Sforzini, Roberta Mussinelli, Vittorio Rosti, Alessandro Lozza, Anna Racchi, Mario Sabatelli, Marco Luigetti, Giulia Bisogni, Ângela Romano, Valeria Guglielmino, Andrea Di Paolantonio, Daniela Bernardo, Giuseppe Vita, Anna Mazzeo, Massimo Russo, Davide Pareyson, Daniela Calabrese, Silvia Fenu, Paola Saveri, Hans L. A. Nienhuis, Geert Bokhorst, C. M. Roos, Margriet Couperus, Greetje de Jong, Anne F. Brunger, Gea Drost, Fiete Lange, Adinda Colauto, Márcia Waddington‐Cruz, Aline França de Abreu, Roberto Coury Pedrosa, Renata Gervais de Santa Rosa, Moisés Dias, Fetra Rakotondratafika, Andoni Echaniz‐Laguna, Cécile Cauquil, Céline Labeyrie, Guillemette Beaudonnet, Yasmine Boubrit, Amina Gaouar, Halima Bourenane, Shahram Attarian, El Khansa Yahia, Annie Verschueren, Aude‐Marie Grapperon, Émilien Delmont, Violaine Planté‐Bordeneuve, Laetitia Vervoitte, Samar S. Ayache, Philippe Le Corvoisier, Raphaele Arrouasse, Thierry Gendre, Laure Abou Chakra, Cécile Focseneanu, Caroline Barau, Guilhem Solé, L. Belin, Marie Helene Violleau, Fanny Duval-Bontemps, Rami Massie, Xin Dong, Francisco Muñoz-Beamud, Sandra García, Cristina Borrachero, Álvaro Gragera Martínez, Lucía Galán Dávila, Marta Palacios, Laura Martínez Vicente, Leopoldo Pérez de Isla, Carlos Casasnovas, Carles Díez‐López, Elena Muñoz Fabra, José González‐Costello, Sonia Guerrero, Sergi Yun, Yurema Martinez, Valentina Vélez-Santamaría, Velina Nedkova-Hristova, Pablo García Pavía, Ariadna González Segovia, Fernando de Frutos, Esther González-López, Fernándo Domínguez, Luis Escobar-López, Eva Cabrera-Romero, Paula Sánchez Gismera, María de la Iglesia, Fernando Martinez Valle, G Aguila, Karen Lorite, N. Raguer, Pilar Suñé, P Piera, Carlos Ortega, Carla Aguilar, Gisela Gili, Hartmut Schmidt, Christel Langenstroer, Anna Hüsing‐Kabar, Iyad Kabar, Matthias Schilling, Frauke Friebel, Phil‐Robin Tepasse, Frank Birklein, Monika Firros, Fabiola Escolano‐Lozano, Caitlin Brueckner, Vanessa Bahnam, Michelle Kaku, K. H. Vincent Lau, Janice F. Wiesman, Martha Grogan, Susanna Miller, Janell Grazzini Frantz, Diane C. Schmidt, Omar F. AbouEzzeddine, Wayne H. Miller, Grace Lin, Morie A. Gertz, Angela Dispenzieri, Thomas H. Brannagan, Raisy Fayerman, Elizabeth DuVerger, Jorge Cabrera, Mathew S. Maurer, Christina Ulane, Louis H. Weimer, Stephen H. Tsang, Jeffrey Shije, Nathan Carberry, Sai Si Thu, Dianna Quan, Brianna Blume, J. Scott Overcash, Pu He, Kia Lee, Hanh Chu, Karla Zepeda, Michael R. Waters, Thao Vuong, Derya J Coskun, Kimberly Quillin, Allison Davis, Michael Polydefkis, Jing Ye, Xiaoling Li, Mohammad Khoshnoodi, Geno Vista, Tae Hwan Chung, Michele Watt, Dan Tsottles, Ahmad Masri, Dayna Carlson, Brian Drachman, Patricia Divito, Hansie Mathelier, Margaret McCloskey Shanks, Karen Maslowski, Sami Khella, J. Pieretti, Benjamin Joslin, Emma Schmidt, Miriam Freimer, Julie Agriesti, Fábio Barroso, F Picone, Andrea Lautre, Lucas Orellana, Wenqin Du, Joost Felius, Alejandra González‐Duarte, Karla Cárdenas‐Soto, Rebecca Traub, Manisha Chopra, Chi‐Chao Chao, Chia-Hua Hsu, Li‐Kai Tsai, Ming‐Jen Lee, Jen-Jen Su, Sung‐Tsang Hsieh, Hsueh‐Wen Hsueh, Hsi-Chieh Chou, Byoung‐Joon Kim, Hyesun Kang, Ju‐Hong Min, Eun‐Seok Jeon, Yeon Hak Chung, Jae Hong Park, Jeeyoung Oh, Hyeon Joo Jeong, Ivailo Tournev, Sashka Zhelyazkova, Yohei Misumi, Yumiko Sakamoto, Nami Hashimoto, Yoshimi Misumi, Aya Takahashi, Mitsuharu Ueda, Teruaki Masuda, Mitsuharu Ueda, Masahisa Katsuno, Kazuki Tajima, Momoko Sumi, Fujiko Hasegawa, Takahiro Okumura, Masahiro Iijima, Yuki Fukami, Daisuke Ito, Yoshiyuki Kishimoto, Tomoyuki Kazuta, Katsuhiko Kato, Naohiro Mouri, Soma Furukawa, Ryoji Nishi, Yoshiki Sekijima, Keiko Ito, Naga-aki Kato, Dai Kishida, Hideki Mochizuki, Kaori Okada, Kurumi Ohashi, Kensuke Ikenaka, Masayuki Nakamori, Makoto Kinoshita, Bella Ruth R. Mapalo, Steven Law, Liza Chacko, Helen J. Lachmann, Oliver Cohen, Yousuf Razvi, Sindhu Varughese, Ana Martinez‐Naharro, Richard W. Orrell, Marianna Fontana, Lisa Rannigan, Sarah Louth, Eleni Zamba‐Papanicolaou, Demetra Charalamnibous, Rana Abu Manneh, Kleopas A. Kleopa, Theodoros Christodoulides, Savvas Frangos,

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