Artigo Acesso aberto Revisado por pares

OC 20.3 Improved Joint Health After Gene Therapy with Dirloctocogene Samoparvovec (SPK-8011) in People with Hemophilia A

2023; Elsevier BV; Volume: 7; Linguagem: Inglês

10.1016/j.rpth.2023.100449

ISSN

2475-0379

Autores

Ben J. Samelson-Jones, Margaret V. Ragni, John E.J. Rasko, Kristina M. Haley, Sara Croteau, Jerome Teitel, Huyen Tran, Peter H. Cygan, Susan Sullivan, Jill Moormeier, Savina Jaeger, Aidan A. Long, G Lévy, Amy MacDougall, Kassie Jaworski, Tiffany Chang,

Tópico(s)

Hemophilia Treatment and Research

Referência(s)