OC 20.3 Improved Joint Health After Gene Therapy with Dirloctocogene Samoparvovec (SPK-8011) in People with Hemophilia A
2023; Elsevier BV; Volume: 7; Linguagem: Inglês
10.1016/j.rpth.2023.100449
ISSN2475-0379
AutoresBen J. Samelson-Jones, Margaret V. Ragni, John E.J. Rasko, Kristina M. Haley, Sara Croteau, Jerome Teitel, Huyen Tran, Peter H. Cygan, Susan Sullivan, Jill Moormeier, Savina Jaeger, Aidan A. Long, G Lévy, Amy MacDougall, Kassie Jaworski, Tiffany Chang,
Tópico(s)Hemophilia Treatment and Research
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