AAV delivers as a lingering guest, not an invader
2024; Elsevier BV; Volume: 143; Issue: 23 Linguagem: Inglês
10.1182/blood.2024024506
ISSN1528-0020
Autores Tópico(s)Neurogenetic and Muscular Disorders Research
ResumoIn this issue of Blood, Batty and colleagues 1 report on hepatic adenoassociated virus vector-factor III (AAV-FIII) integration and fate more than 10 years after AAV gene delivery in dogs with hemophilia A (HA).
Referência(s)