Five-Year Results With Patisiran for Hereditary Transthyretin Amyloidosis With Polyneuropathy

American Medical Association;

Autores

David Adams, Jonas Wixner, Michael Polydefkis, John L. Berk, Isabel Conceição, Angela Dispenzieri, Amanda Peltier, Mitsuharu Ueda, Shaun Bender, Kelley E. Capocelli, Patrick Y. Jay, Elena Yureneva, Laura Obici, Gian Luca Vita, Vincenzo Rizzo, Massimo Russo, Anna Mazzeo, Luca Gentile, John L. Berk, Janice F. Wiesman, Michelle Kaku, Vincent Lau, Douglas DeLong, James A. R. Dalton, John J. May, Shahram Attarian, Émilien Delmont, Jean Pouget, Annie Verschueren, Aude‐Marie Grapperon, Emmanuelle Salort‐Campana, Isabel Conceição, Carlos Marques‐Neves, Miguel Oliveira Santos, Conceição de Azevedo Coutinho, Catarina Falcão de Campos, Teresa Coelho, Antonio Hipólito Reis, Nuno Correia, Javier Martínez Pérez, Ângela Silva, Cristina Alves, Márcio Cardoso, Kátia Valdrez, Julia R Monte, Marta Novais, Nádia Guimarães, Inês Cardoso, Mónica Freitas, Joana Ramalho, Natália Ferreira, Daisuke Kuzume, Masahiro Yamasaki, Yuko Morimoto, Céline Tard, É. Hachulla, Clément Gauvain, Maria-Claire Migaud-Chervy, Dominique Deplanque, Elsa Jozefowicz, Loïc Lebellec, David Adams, Marie Théaudin-Saliou, Cécile Cauquil-Michon, Céline Labeyrie, Adeline Not, Abdallah Al‐Salameh, Anne-Lise Lecoq, Maeva Stephant, Andoni Echaniz‐Laguna, Laurent Becquemont, Guillemette Beaudonnet, Vincent Algalarrondo, Ludivine Eliahou, Michel Slama, Antoine Rousseau, Aïssatou Signaté, Paola Darche, Jérôme Grimaud, Emeline Berthelot, Jocelyn Inamo, Violaine Planté‐Bordeneuve, Thierry Gendre, Raphaele Arrouasse, Samar S. Ayache, Laura Ernande, Philippe Le Corvoisier, Hayet Salhi, Ariane Choumert, Cyril Charlin, Thomas Megelin, Thomas H. Brannagan, Steven Tsang, Fernanda Wajnsztajn, Jeffrey Shije, Christina Ulane, Inna Kleyman, Louis H. Weimer, Comana Cioroiu, Kleopas A. Kleopa, Eleni Zamba‐Papanicolaou, Satoshi Tada, Masahiro Nagai, Rina Ando, Yuki Yamanishi, J. Scott Overcash, Sinikka Green, Michael R. Waters, Derya J Coskun, Paul S. Manos, Karla A Zepeda, William O’Riordan, Laura Obici, Andrea Cortese, Alessandro Lozza, Giampaolo Merlini, Vittorio Rosti, Mario Sabatelli, Giulia Bisogni, Daniela Bernardo, Marco Luigetti, Andrea Di Paolantonio, Valeria Guglielmino, Ângela Romano, Hans Nienhuis, Arnt V. Kristen, Christian Nagel, Fabian aus dem Siepen, Selina Hein, Shuichiro Neshige, Josep M. Campistol, Lida María Rodas Marín, Josep Miquel Blasco Pelicano, Lucía Galán Dávila, Vanesa Pytel Cordoba, A. Guerrero Sola, Alejandro Horga, J. García–Sánchez, Leopoldo Pérez de Isla, Wilson Marques, Carolina Lavigne Moreira, Vanessa Daccach Marques, Francisco Muñoz Beamud, Cristina Borrachero, Iván A. López, Mónica Sanz, E Oliver, Juan González Moreno, J. Michael Martinez, Cristina Descals, Mercedes Usón, Francisco Jose Vega, Antoni Figuerola, Carles Montalá, Márcia Waddington‐Cruz, Aline França de Abreu, Moisés Dias, Renata Gervais de Santa Rosa, Marcus Vinícius Pinto, Amanda Cardoso Berensztejn, Luiz Felipe Pinto, Mariana de Andrade Guedes, Fábio Barroso, Andrea Lautre, Lucas Orellana, Maria Alejandra González-Duarte Briseño, Karla Cárdenas‐Soto, Carlos Cantú‐Brito, David Rivera de la Parra, Jose Pablo Hernandez Reyes, Maria del Mar Saniger Alba, Yeşim Parman, Erdi Şahin, Nail Güven Serbest, Hacer Durmuş, Arman Çakar, Saçit Karamürsel, Ali Elitok, Nermin G Sirin Inan, Emre Altinkurt, Michael Polydefkis, Adriane C Allen, Vinay Chaudhry, R. J. Jarrett, Neil M. Bressler, Mandeep Singh, Mohammad Khoshnoodi, Daniel P. Judge, A. T. Y. Lui, Tae Hwan Chung, Geno Vista, Syed Mahmood Shah, Hirotoshi Hamaguchi, Tetsuya Oda, Masahiro Shimomura, Christof Scheid, Udo Holtick, Jeeyoung Oh, Han Jo Kim, Hyun Jin Shin, Kyomin Choi, Mitsuharu Ueda, Yohei Misumi, Toshiya Nomura, Takahisa Tateishi, Elizabeth A. Mauricio, Elliot L. Dimberg, Leslie T. Cooper, Angela Dispenzieri, Amie Fonder, Miriam Hobbs, P. James B. Dyck, Wilson I. Gonsalves, Nelson Leung, Thomas E. Witzig, Yi L. Hwa, Prashant Kapoor, Shaji Kumar, Yi Lin, S. Vincent Rajkumar, David Dingli, Morie A. Gertz, P. James B. Dyck, Linde E. Gove, Samir Dalia, David Croy, Tim Holding, Peter D. Gorevic, Chi‐Chao Chao, Ming‐Jen Lee, Jen-Jen Su, Sung‐Tsang Hsieh, Li‐Kai Tsai, Shin‐Joe Yeh, Chih‐Chao Yang, Chao-Wen Lin, Senda Ajroud‐Driss, Robert Sufit, John-Michael Li, Miriam Freimer, Samantha LoRusso, Yasuhiro Aso, Byoung‐Joon Kim, JuHyeon Kim, Ga-Yeon Lee, Eun Bin Cho, Eun‐Seok Jeon, Ju‐Hong Min, Jin Myoung Seok, Hye Lim Lee, Jae Hong Park, Yoshiki Sekijima, Naga-aki Kato, Dai Kishida, Akiyo Hineno, Minori Kodaira, Tsuneaki Yoshinaga, Ken Takasone, Teruyoshi Miyahara, Yusuke Takahashi, Akira Imai, Kazuhiko Matsumoto, Kon-Ping Lin, Yi‐Chung Lee, Jonas Wixner, Björn Pilebro, Ole B. Suhr, Intissar Anan, Erik Nordh, Fátima Pedrosa Domellöf, Maria Chermenina, Anneli Nygren, Ivaylo Tournev, Sashka Zhelyazkova, Zheyna Cherneva, S. Sarafov, Teodora Chamova, Sylvia Cherninkova-Gopina, Hartmut Schmidt, Elena Vorona, Anna Huesing-Kabar, Matthias Schilling, Iyad Kabar, Phil‐Robin Tepasse, Julian D. Gillmore, Ana Martinez‐Naharro, Liza Chacko, Oliver Cohen, Steven Law, Tamer Rezk, Helen J. Lachmann, Dianna Quan, Stacy Dixon, Vera Fridman, Soon-Chai Low, Khean Jin Goh,

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